The most expensive injection in the world: Ukraine for the first time received a rare drug for children with SMA

Ukraine for the first time received a rare drug Spinraza. It is one of three drugs available in the world that are used during the treatment of children with spinal muscular atrophy.

As stated on the website of the Ministry of Health of Ukraine, more than 150 vials of the drug have already been delivered to thirteen hospitals in the country.

Why is this drug important?

Spinal muscular atrophy is one of the rarest genetic diseases characterized by progressive muscle weakness throughout the body.

With age, it leads to a violation of the musculoskeletal system and ultimately chains the patient to a wheelchair and bed.

However, SMA is the most common genetic cause of death in children. According to statistics, this disease affects one or two babies out of 10 thousand newborns.

In Ukraine today more than 200 children have a confirmed diagnosis of spinal muscular atrophy.

“Today, without exaggeration, is an important day in the history of Ukrainian medicine. We did not just receive expensive medicines that have never been available in Ukraine before. We received the most valuable thing – the opportunity to save the lives of children suffering from rare orphan diseases. We thank the donors who donated for our children this chance for life,” says Deputy Minister of Health Marija Karčević.

What is Spinraza

Spinraza is a drug registered by the American company Biogen, which is administered by injection directly into the cerebrospinal fluid through the lower back.

Maintenance injections are needed throughout life – six injections in the first year and three injections annually thereafter

This medicine is called the most expensive injection in the world, since one bottle of Spinraza costs more than 100 thousand dollars, which is about three million hryvnias.

Germany, Italy, Croatia, Austria, Denmark, Luxembourg, Switzerland, France, Japan, Israel, Turkey, Sweden, Spain, USA, Brazil and South Korea provide this drug free of charge to their citizens. And from now on there will be Ukraine.

What are the analogues

There are three drugs in the world that are used to treat SMA:

  • Zolgensma
  • Evrysdi
  • Spinraza.

The first is administered before the age of two and repairs the SMN1 gene, stopping the disease forever.

The last two should be applied throughout life.

Earlier, doctors found out how many years Ukrainians will grow old

because of the war .

Also read which doctor Ukrainians most often turn to during the war .

WE NEED YOU AT THIS CRUCIAL TIME IN OUR COUNTRY, THOUSANDS ARE DISPLACED WITH A DAILY INCREASE IN THE NUMBER OF CASUALTIES FROM THE RUSSIA WAR AGAINST UKRAINE.

YOU CAN HELP US WIN, PROVIDE MEDICAL AID AND CARE FOR THE REFUGEES BY SUPPORTING TOGETHER24 PROJECT WITH YOUR DONATIONS. FROM AS LITTLE AS $1 A GREAT IMPACT CAN BE MADE IN WINNING THIS WAR.

TOGETHER WITH YOU, UKRAINE WILL PREVAIL.

 

Share

Leave a Reply

Your email address will not be published.